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Rare Disease Treatments
Rare Disease Treatments

Pharmaceutical and biotech companies developing orphan drugs and therapies for rare diseases affecting small patient populations

Symbols
LLY
LLYLilly(Eli) & CoMarket Cap: $921.5B
ABBV
ABBVAbbvie IncMarket Cap: $410.7B
NOVN
NOVNNovartis AGMarket Cap: $260.5B
NVO
NVONovo NordiskMarket Cap: $217.7B
AMGN
AMGNAMGEN Inc.Market Cap: $181.3B
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $110.9B
KPTI
KPTIKaryopharm Therapeutics IncMarket Cap: $96.8B
BRM
BRMBristol-Myers Squibb Co.Market Cap: $95B
BMY
BMYBristol-Myers Squibb Co.Market Cap: $95B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $72.9B
SNY
SNYSanofiMarket Cap: $65.9B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $59.3B
ARGX
ARGXArgen X SEMarket Cap: $55.2B
INSM
INSMInsmed IncMarket Cap: $41.2B
EDG
EDGGold Fields LtdMarket Cap: $36.5B
ZLAB
ZLABZai Lab LimitedMarket Cap: $31.8B
BIIB
BIIBBiogen IncMarket Cap: $24.6B
TAK
TAKTakeda Pharmaceutical CoMarket Cap: $24.3B
INCY
INCYIncyte Corp.Market Cap: $20.4B
UTHR
UTHRUnited Therapeutics CorpMarket Cap: $20.1B