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Rare Disease Treatments
Rare Disease Treatments

Pharmaceutical and biotech companies developing orphan drugs and therapies for rare diseases affecting small patient populations

Theme performance
Symbols
LLY
LLYLilly(Eli) & CoMarket Cap: $1.1T
ABBV
ABBVAbbvie IncMarket Cap: $468.2B
NOVN
NOVNNovartis AGMarket Cap: $303.1B
AMGN
AMGNAMGEN Inc.Market Cap: $237.5B
NVO
NVONovo NordiskMarket Cap: $208.7B
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $138.9B
BRM
BRMBristol-Myers Squibb Co.Market Cap: $136.9B
BMY
BMYBristol-Myers Squibb Co.Market Cap: $136.9B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $85.9B
ARGX
ARGXArgen X SEMarket Cap: $64.3B
MRNA
MRNAModerna IncMarket Cap: $57.9B
SNY
SNYSanofiMarket Cap: $55.9B
EDG
EDGGold Fields LtdMarket Cap: $37.1B
BIIB
BIIBBiogen IncMarket Cap: $32B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $31.6B
TAK
TAKTakeda Pharmaceutical CoMarket Cap: $31.3B
INSM
INSMInsmed IncMarket Cap: $27.5B
ROIV
ROIVRoivant Sciences LtdMarket Cap: $26.2B
INCY
INCYIncyte Corp.Market Cap: $25.9B
UTHR
UTHRUnited Therapeutics CorpMarket Cap: $22B