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Rare Disease Treatments
Rare Disease Treatments

Pharmaceutical and biotech companies developing orphan drugs and therapies for rare diseases affecting small patient populations

Symbols
LLY
LLYLilly(Eli) & CoMarket Cap: $844.9B
ABBV
ABBVAbbvie IncMarket Cap: $367.7B
NOVN
NOVNNovartis AGMarket Cap: $294B
AMGN
AMGNAMGEN Inc.Market Cap: $189.2B
NVO
NVONovo NordiskMarket Cap: $169.2B
BRM
BRMBristol-Myers Squibb Co.Market Cap: $119.4B
BMY
BMYBristol-Myers Squibb Co.Market Cap: $119.4B
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $110.8B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $79.2B
SNY
SNYSanofiMarket Cap: $57B
ARGX
ARGXArgen X SEMarket Cap: $49.5B
EDG
EDGGold Fields LtdMarket Cap: $44.2B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $42.7B
INSM
INSMInsmed IncMarket Cap: $33.4B
TAK
TAKTakeda Pharmaceutical CoMarket Cap: $30.7B
BDRX
BDRXBiodexa Pharmaceuticals PlcMarket Cap: $30.3B
ZLAB
ZLABZai Lab LimitedMarket Cap: $29.2B
BIIB
BIIBBiogen IncMarket Cap: $25.4B
UTHR
UTHRUnited Therapeutics CorpMarket Cap: $25.1B
ROIV
ROIVRoivant Sciences LtdMarket Cap: $20.2B