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Rare Disease Treatments
Rare Disease Treatments

Pharmaceutical and biotech companies developing orphan drugs and therapies for rare diseases affecting small patient populations

Symbols
LLY
LLYLilly(Eli) & CoMarket Cap: $1.1T
ABBV
ABBVAbbvie IncMarket Cap: $438.3B
NOVN
NOVNNovartis AGMarket Cap: $294B
NVO
NVONovo NordiskMarket Cap: $220.9B
AMGN
AMGNAMGEN Inc.Market Cap: $196.1B
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $123.2B
BRM
BRMBristol-Myers Squibb Co.Market Cap: $117.6B
BMY
BMYBristol-Myers Squibb Co.Market Cap: $117.6B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $69.7B
ARGX
ARGXArgen X SEMarket Cap: $54.3B
SNY
SNYSanofiMarket Cap: $53B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $39.9B
RDHL
RDHLRedhill Biopharma Ltd.Market Cap: $35.4B
EDG
EDGGold Fields LtdMarket Cap: $30.6B
BIIB
BIIBBiogen IncMarket Cap: $29.4B
TAK
TAKTakeda Pharmaceutical CoMarket Cap: $28.5B
MRNA
MRNAModerna IncMarket Cap: $27.1B
ROIV
ROIVRoivant Sciences LtdMarket Cap: $25.9B
INSM
INSMInsmed IncMarket Cap: $25.1B
INCY
INCYIncyte Corp.Market Cap: $23.3B