Rare Disease Treatments
Pharmaceutical and biotech companies developing orphan drugs and therapies for rare diseases affecting small patient populations
Symbols
LLYLilly(Eli) & CoMarket Cap: $1T
ABBVAbbvie IncMarket Cap: $405.3B
NOVNNoven Pharmaceuticals, Inc.Market Cap: $272.3B
NVONovo NordiskMarket Cap: $236.3B
AMGNAMGEN Inc.Market Cap: $176.4B
KPTIKaryopharm Therapeutics IncMarket Cap: $122.6B
VRTXVertex Pharmaceuticals, Inc.Market Cap: $114.7B
BMYBristol-Myers Squibb Co.Market Cap: $108.8B
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $81.6B
SNYSanofiMarket Cap: $60.9B
ALNYAlnylam Pharmaceuticals IncMarket Cap: $52.9B
ARGXArgen X SEMarket Cap: $51B
EDGEdgen Group IncMarket Cap: $41.3B
INSMInsmed IncMarket Cap: $37.8B
TAKTakeda Pharmaceutical CoMarket Cap: $26.5B
BIIBBiogen IncMarket Cap: $26.1B
ZLABZai Lab LimitedMarket Cap: $25.3B
UTHRUnited Therapeutics CorpMarket Cap: $21.4B
INCYIncyte Corp.Market Cap: $19.9B
ROIVRoivant Sciences LtdMarket Cap: $15.3B