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Rare Disease Treatments
Rare Disease Treatments

Pharmaceutical and biotech companies developing orphan drugs and therapies for rare diseases affecting small patient populations

Symbols
LLY
LLYLilly(Eli) & CoMarket Cap: $1T
ABBV
ABBVAbbvie IncMarket Cap: $381.1B
NOVN
NOVNNovartis AGMarket Cap: $290.1B
NVO
NVONovo NordiskMarket Cap: $202.8B
AMGN
AMGNAMGEN Inc.Market Cap: $183.1B
BRM
BRMBristol-Myers Squibb Co.Market Cap: $121.4B
BMY
BMYBristol-Myers Squibb Co.Market Cap: $121.4B
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $110.3B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $67B
SNY
SNYSanofiMarket Cap: $54B
ARGX
ARGXArgen X SEMarket Cap: $49.9B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $39.7B
EDG
EDGGold Fields LtdMarket Cap: $35.4B
BDRX
BDRXBiodexa Pharmaceuticals PlcMarket Cap: $29.6B
BIIB
BIIBBiogen IncMarket Cap: $28.6B
TAK
TAKTakeda Pharmaceutical CoMarket Cap: $27.6B
ZLAB
ZLABZai Lab LimitedMarket Cap: $27.2B
UTHR
UTHRUnited Therapeutics CorpMarket Cap: $24.1B
INSM
INSMInsmed IncMarket Cap: $23B
ROIV
ROIVRoivant Sciences LtdMarket Cap: $21.5B