Gene Therapy
Gene therapy, gene editing, CRISPR, and genetic medicine
Theme performance
Symbols
VRTXVertex Pharmaceuticals, Inc.Market Cap: $138.9B
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $85.9B
ALNYAlnylam Pharmaceuticals IncMarket Cap: $31.6B
BMRNBiomarin Pharmaceutical Inc.Market Cap: $12.9B
KRYSKrystal Biotech IncMarket Cap: $10.3B
DNTHDianthus Therapeutics IncMarket Cap: $6.2B
PTCTPTC Therapeutics IncMarket Cap: $5.8B
CRSPCRISPR Therapeutics AGMarket Cap: $5.8B
QUREuniQure N.V.Market Cap: $3.4B
BEAMBeam Therapeutics IncMarket Cap: $3.1B
PGENPrecigen IncMarket Cap: $2.6B
RAREUltragenyx Pharmaceutical Inc.Market Cap: $2.5B
MRVIMaravai LifeSciences Holdings IncMarket Cap: $2.2B
SRPTSarepta Therapeutics IncMarket Cap: $2B
TSHATaysha Gene Therapies IncMarket Cap: $2B
BLFSBiolife Solutions IncMarket Cap: $1.8B
NTLAIntellia Therapeutics IncMarket Cap: $1.8B
VORVor Biopharma IncMarket Cap: $1.4B
MGTXMeiraGTx Holdings plcMarket Cap: $1.4B
SANASana Biotechnology IncMarket Cap: $1.2B