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Gene Therapy
Gene Therapy

Gene therapy, gene editing, CRISPR, and genetic medicine

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Symbols
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $128.2B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $76.4B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $30B
BMRN
BMRNBiomarin Pharmaceutical Inc.Market Cap: $10.7B
KRYS
KRYSKrystal Biotech IncMarket Cap: $9.6B
CRSP
CRSPCRISPR Therapeutics AGMarket Cap: $5.1B
PTCT
PTCTPTC Therapeutics IncMarket Cap: $5.3B
DNTH
DNTHDianthus Therapeutics IncMarket Cap: $4.7B
PGEN
PGENPrecigen IncMarket Cap: $2.7B
BEAM
BEAMBeam Therapeutics IncMarket Cap: $2.6B
MRVI
MRVIMaravai LifeSciences Holdings IncMarket Cap: $1.9B
SRPT
SRPTSarepta Therapeutics IncMarket Cap: $1.8B
BLFS
BLFSBiolife Solutions IncMarket Cap: $1.9B
NTLA
NTLAIntellia Therapeutics IncMarket Cap: $1.6B
QURE
QUREuniQure N.V.Market Cap: $1.6B
TSHA
TSHATaysha Gene Therapies IncMarket Cap: $1.4B
RARE
RAREUltragenyx Pharmaceutical Inc.Market Cap: $1.5B
VOR
VORVor Biopharma IncMarket Cap: $1.1B
MGTX
MGTXMeiraGTx Holdings plcMarket Cap: $1B
VERV
VERVVerve Therapeutics IncMarket Cap: $1B