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Gene Therapy
Gene Therapy

Gene therapy, gene editing, CRISPR, and genetic medicine

Symbols
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $110.8B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $79.2B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $42.7B
BMRN
BMRNBiomarin Pharmaceutical Inc.Market Cap: $10.5B
KRYS
KRYSKrystal Biotech IncMarket Cap: $7.6B
PTCT
PTCTPTC Therapeutics IncMarket Cap: $5.7B
CRSP
CRSPCRISPR Therapeutics AGMarket Cap: $4.9B
DNTH
DNTHDianthus Therapeutics IncMarket Cap: $4B
BEAM
BEAMBeam Therapeutics IncMarket Cap: $2.8B
RARE
RAREUltragenyx Pharmaceutical Inc.Market Cap: $2.3B
SRPT
SRPTSarepta Therapeutics IncMarket Cap: $2.2B
NTLA
NTLAIntellia Therapeutics IncMarket Cap: $1.6B
PGEN
PGENPrecigen IncMarket Cap: $1.5B
WVE
WVEWave Life Sciences Ltd.Market Cap: $1.4B
TSHA
TSHATaysha Gene Therapies IncMarket Cap: $1.3B
VERV
VERVVerve Therapeutics IncMarket Cap: $1B
QURE
QUREuniQure N.V.Market Cap: $1B
BLFS
BLFSBiolife Solutions IncMarket Cap: $1B
SANA
SANASana Biotechnology IncMarket Cap: $824.6M
MRVI
MRVIMaravai LifeSciences Holdings IncMarket Cap: $789.2M