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Gene Therapy
Gene Therapy

Gene therapy, gene editing, CRISPR, and genetic medicine

Symbols
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $110.3B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $67B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $39.7B
BMRN
BMRNBiomarin Pharmaceutical Inc.Market Cap: $10.5B
KRYS
KRYSKrystal Biotech IncMarket Cap: $8.8B
CRSP
CRSPCRISPR Therapeutics AGMarket Cap: $4.9B
DNTH
DNTHDianthus Therapeutics IncMarket Cap: $4.7B
BEAM
BEAMBeam Therapeutics IncMarket Cap: $2.9B
RARE
RAREUltragenyx Pharmaceutical Inc.Market Cap: $2.3B
SRPT
SRPTSarepta Therapeutics IncMarket Cap: $1.8B
NTLA
NTLAIntellia Therapeutics IncMarket Cap: $1.8B
TSHA
TSHATaysha Gene Therapies IncMarket Cap: $1.6B
QURE
QUREuniQure N.V.Market Cap: $1.5B
PGEN
PGENPrecigen IncMarket Cap: $1.5B
WVE
WVEWave Life Sciences Ltd.Market Cap: $1.2B
BLFS
BLFSBiolife Solutions IncMarket Cap: $1.2B
MRVI
MRVIMaravai LifeSciences Holdings IncMarket Cap: $1.1B
MGTX
MGTXMeiraGTx Holdings plcMarket Cap: $855.7M
SANA
SANASana Biotechnology IncMarket Cap: $854.4M
VOR
VORVor Biopharma IncMarket Cap: $776.5M