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Gene Therapy
Gene Therapy

Gene therapy, gene editing, CRISPR, and genetic medicine

Symbols
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $123.2B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $69.7B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $39.9B
BMRN
BMRNBiomarin Pharmaceutical Inc.Market Cap: $11.4B
KRYS
KRYSKrystal Biotech IncMarket Cap: $10.8B
DNTH
DNTHDianthus Therapeutics IncMarket Cap: $5.3B
CRSP
CRSPCRISPR Therapeutics AGMarket Cap: $5.1B
BEAM
BEAMBeam Therapeutics IncMarket Cap: $3.4B
RARE
RAREUltragenyx Pharmaceutical Inc.Market Cap: $3.3B
QURE
QUREuniQure N.V.Market Cap: $2.7B
SRPT
SRPTSarepta Therapeutics IncMarket Cap: $2B
NTLA
NTLAIntellia Therapeutics IncMarket Cap: $2B
PGEN
PGENPrecigen IncMarket Cap: $1.9B
TSHA
TSHATaysha Gene Therapies IncMarket Cap: $1.8B
MRVI
MRVIMaravai LifeSciences Holdings IncMarket Cap: $1.6B
BLFS
BLFSBiolife Solutions IncMarket Cap: $1.4B
MGTX
MGTXMeiraGTx Holdings plcMarket Cap: $1.2B
WVE
WVEWave Life Sciences Ltd.Market Cap: $1.2B
SANA
SANASana Biotechnology IncMarket Cap: $1.1B
VOR
VORVor Biopharma IncMarket Cap: $1B