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Gene Therapy
Gene Therapy

Gene therapy, gene editing, CRISPR, and genetic medicine

Symbols
VRTX
VRTXVertex Pharmaceuticals, Inc.Market Cap: $110.9B
REGN
REGNRegeneron Pharmaceuticals, Inc.Market Cap: $72.9B
ALNY
ALNYAlnylam Pharmaceuticals IncMarket Cap: $59.3B
BMRN
BMRNBiomarin Pharmaceutical Inc.Market Cap: $10.5B
PTCT
PTCTPTC Therapeutics IncMarket Cap: $6B
KRYS
KRYSKrystal Biotech IncMarket Cap: $6B
CRSP
CRSPCRISPR Therapeutics AGMarket Cap: $5B
RARE
RAREUltragenyx Pharmaceutical Inc.Market Cap: $3.2B
BEAM
BEAMBeam Therapeutics IncMarket Cap: $2.2B
SRPT
SRPTSarepta Therapeutics IncMarket Cap: $2B
QURE
QUREuniQure N.V.Market Cap: $1.9B
DNTH
DNTHDianthus Therapeutics IncMarket Cap: $1.8B
PGEN
PGENPrecigen IncMarket Cap: $1.7B
WVE
WVEWave Life Sciences Ltd.Market Cap: $1.2B
BLFS
BLFSBiolife Solutions IncMarket Cap: $1.2B
TSHA
TSHATaysha Gene Therapies IncMarket Cap: $1.1B
SANA
SANASana Biotechnology IncMarket Cap: $1.1B
NTLA
NTLAIntellia Therapeutics IncMarket Cap: $1B
VERV
VERVVerve Therapeutics IncMarket Cap: $1B
MRVI
MRVIMaravai LifeSciences Holdings IncMarket Cap: $930.8M